DUCHENNE MUSCULAR DYSTROPHY. “Nearly 20 years ago, when the teenaged Tabebordbar learned that just one gene was at the root of most genetic muscle diseases, he thought fixing it should be simple. “We know what gene is defective,” he says. “If we can just replace that one gene, that would be it. So why is it taking so long?” This was the mantra 20 years ago, I used to say it myself.
https://lnkd.in/d-fHXvT2
linkedin post 2022-06-29 05:12:48
Nigel Fleming
September 21, 2022